A new CRISPR-based one-off procedure that lowers "bad" cholesterol has been approved to enter Phase I human trial. If ...
Dr. Rebecca Ahrens-Nicklas and Dr. Kiran Musunru crafted a bespoke treatment that has successfully corrected the genetic ...
With a shared purpose, we can realize the true promise of CRISPR and improve healthcare, providing hope to more patients with ...
Explore groundbreaking gene-editing therapy for kidney disease, offering hope to those with polycystic kidney disease.
In cellular and animal models of neuroblastoma, small cell lung cancer and colon cancer, this strategy reduces tumours, ...
Regeneron Pharmaceuticals is committing $150 million to begin an alliance on a Tessera Therapeutics gene-editing medicine nearing the clinic as a potential treatment for a rare disease that leads to ...
David Liu and Richard Merkin of the Broad Institute of MIT and Harvard, along with Columbia professor Sam Sternberg, have developed a new, targeted means of inserting entire genes into human DNA ...
Greer, South Carolina, family hosts fundraiser for gene therapy to treat children with rare disorder
IS HOLDING A FUNDRAISER TO HELP TWO OF THEIR CHILDREN. BOTH CHILDREN HAVE A GENETIC DISORDER THAT, AMONG OTHER THINGS, CAUSES A FLOOD OF SEIZURES. AND THE ANSWER TO THE PROBLEM MAY LIE IN A GENE ...
Doctors announced this week that they have treated a newborn baby with a rare genetic disease using the world’s first personalized gene editing therapy. Geoff Bennett discussed the treatment and its ...
PORTLAND, Ore. — Doctors at OHSU’s Casey Eye Institute recently replaced defective DNA with normal DNA on a live patient. It’s part of a clinical trial called Brilliance, which is designed to bring ...
Scientists have corrected gene mutations in mice causing an ultra-rare disease by editing DNA directly in the brain with a single injection, a feat with profound implications for patients with ...
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